Neoantigen peptide vaccines
NeoVax, NEO-PV-01, personalised neoantigen long-peptide vaccine, patient-specific synthetic long peptide vaccine; related mRNA context: autogene cevumeran (BNT122/RO7198457), individualised neoantigen therapy (mRNA-4157/V940)
1What it is
This is the current frontier of therapeutic cancer vaccination, and the honest framing is that it is a strong idea with thin randomised evidence. Every tumour carries somatic mutations; a fraction of those produce peptides that the patient's HLA molecules can present and that T cells can recognise. These are neoantigens — genuinely foreign sequences, absent from normal tissue, against which no thymic tolerance exists. Where profiles 231 through 236 targeted shared self-antigens that the immune system has been trained to ignore, this approach manufactures a different vaccine for every patient.
The practical pipeline is: sequence the tumour and matched normal DNA, call the mutations, predict which resulting peptides will bind the patient's HLA alleles, rank them, synthesise the best 10–20 as long peptides, and vaccinate with a strong adjuvant. Long peptides are used deliberately — they must be taken up and processed by professional antigen-presenting cells rather than binding HLA directly on any passing cell, which is the mechanism by which short class I peptides (profile 231) can induce tolerance instead of immunity.
The same neoantigen concept is also being delivered as mRNA rather than peptide — autogene cevumeran and mRNA-4157 are the leading examples — and it is important not to conflate the two evidence streams. The peptide route has the longer immunological follow-up; the mRNA route has produced the first randomised efficacy signals.
2How it's thought to work
3What the research shows
Melanoma, adjuvant, peptide vaccine
Glioblastoma, peptide vaccine
Combination with checkpoint blockade
Randomised evidence, from the mRNA route
What has not been shown — stated plainly
4Reported side effects and interactions
Literature-reported
the safety profile across studies has been notably mild for an oncology intervention — injection-site reactions (common, sometimes with persistent nodules), flu-like symptoms, fatigue, low-grade fever, myalgia, transient rash. Poly-ICLC accounts for most of the systemic reactogenicity. No vaccine-attributed grade 3–4 immune toxicity has been consistently reported, and no autoimmune disease caused by neoantigen vaccination has been described. When given with checkpoint inhibitors, immune-related adverse events occur at the rate expected from the checkpoint inhibitor.Community-reported
Community use: essentially none documented. These products cannot exist outside a sequencing-and-manufacturing pipeline tied to an individual patient's tumour.Theoretical. a predicted neoantigen could cross-react with a similar self-peptide and cause autoimmunity; this has been a theoretical concern throughout and has not materialised. Epitope spreading means the eventual response is wider than what was deliberately administered, which is the intended benefit and also the least controllable aspect.
Interactions. corticosteroids, especially dexamethasone, substantially blunt the response and this has been directly observed in the glioblastoma data — the most clinically actionable interaction in this profile. Cytotoxic chemotherapy and lymphodepletion reduce the available T-cell pool. Checkpoint inhibitors are studied as deliberate partners.
Markers researchers commonly monitor
From trial protocols:
| Marker | Why it's watched |
|---|---|
| Tumour mutational burden and whole-exome/RNA sequencing output | determines whether a usable vaccine can be designed at all; low-mutation tumours yield few candidate neoantigens. |
| HLA genotype (class I and II) | required for epitope prediction, not as a restriction on eligibility. |
| Neoantigen-specific CD4+ and CD8+ T-cell frequency over time (ELISpot, tetramer, single-cell TCR sequencing) | the pharmacodynamic readout, and the main scientific output of this field to date. |
| Epitope spreading (responses to non-vaccine mutations) | tracked as evidence that the vaccine initiated a broader process. |
| T-cell receptor clonality in blood and in post-vaccination tumour tissue | used to show vaccine-induced clones actually reach the tumour; the strongest mechanistic evidence available. |
| Circulating tumour DNA | the practical minimal-residual-disease endpoint in adjuvant trials, and probably the surrogate that will make randomised trials feasible. |
| Corticosteroid exposure, particularly dexamethasone | tracked as a covariate because it demonstrably suppresses the response. |
| Recurrence-free and overall survival with protocol imaging | the endpoints that have not yet been met in a randomised peptide-vaccine trial. |
| CBC, CMP, thyroid function and the standard immune-related adverse event panel | when a checkpoint inhibitor is part of the regimen. |
Free for everyone. Safety information is never behind a paywall.
5Formulation and administration context
Each vaccine is manufactured for one patient: tumour and normal tissue are sequenced, candidate neoantigens predicted and ranked, peptides synthesised to clinical grade, quality-tested and released — historically a 10–16 week process, and a central reason this approach is studied after surgery rather than in progressive disease. Doses are given subcutaneously or intradermally by trained staff, with the peptide pool split into several injection groups across different limbs so that multiple draining lymph-node basins are engaged, each with poly-ICLC. Priming doses are front-loaded over the first weeks with boosters months later. Steroid use is restricted by protocol wherever possible. There is no self-prepared, compounded or off-the-shelf version of a personalised vaccine, by definition, and no dose calculation appropriate to publish.
6Commonly studied alongside
Poly-ICLC (the standard adjuvant in this class); pembrolizumab, nivolumab and atezolizumab; mFOLFIRINOX and other adjuvant chemotherapy backbones. Conceptually related: KRAS-targeted peptide vaccines (profile 237) — the shared-neoantigen version of the same idea; IMA901 and GAPVAC (profile 236) — the warehouse-personalised predecessor; gp100 peptide vaccine (profile 231) — the short-peptide approach this class was designed to replace.
Informational cross-links. Not stack recommendations.
7Regulatory status by region
| Region | Status (checked —) |
|---|---|
| United States | Not FDA-approved; investigational. Breakthrough therapy designation has been reported for an mRNA individualised neoantigen therapy in melanoma, which is a different product class from the peptide vaccines profiled here † |
| European Union | Not authorised |
| United Kingdom | Not licensed. A national programme to enrol patients into personalised cancer vaccine trials has been established † |
| Australia | Not approved |
| South Africa | Not registered with SAHPRA |
| Sport | Not listed by WADA; no performance application |
8Open questions
- Will a randomised trial of a personalised neoantigen peptide vaccine ever be run, or has the field moved decisively to mRNA delivery?
- How accurate is neoantigen prediction? A large fraction of predicted epitopes generate no detectable response, and the field still cannot reliably pick the ones that matter.
- Can manufacturing time be reduced enough to treat anything other than minimal residual disease?
- Why is the response so CD4-dominated, and does that matter for killing tumour cells?
9References
- 1Ott PA et al. (2017). An immunogenic personal neoantigen vaccine for patients with melanoma. Nature. PubMed · DOI
- 2Hu Z et al. (2021). Personal neoantigen vaccines induce persistent memory T cell responses and epitope spreading in patients with melanoma. Nature Medicine. PubMed · DOI
- 3Keskin DB et al. (2019). Neoantigen vaccine generates intratumoral T cell responses in phase Ib glioblastoma trial. Nature. PubMed · DOI
- 4Sahin U et al. (2017). Personalized RNA mutanome vaccines mobilize poly-specific therapeutic immunity against cancer. Nature. PubMed · DOI
- 5Rojas LA et al. (2023). Personalized RNA neoantigen vaccines stimulate T cells in pancreatic cancer. Nature. PubMed · DOI
- 6Ott PA et al. (2020). A phase Ib trial of personalized neoantigen therapy plus anti-PD-1 in patients with advanced melanoma, non-small cell lung cancer, or bladder cancer. Cell. PubMed · DOI
- 7Weber JS et al. (2024). Individualised neoantigen therapy mRNA-4157 (V940) plus pembrolizumab versus pembrolizumab monotherapy in resected melanoma (KEYNOTE-942): a randomised, phase 2b study. Lancet. PubMed · DOI
† Being confirmed by our reviewers against current sources.
10Community
Threads and protocols are visible to members. Joining is free.
Self-reported side effects Phase 2
11Page history
Licensed CC BY-NC-SA 4.0. Found an error? Report it · Editorial standards — corrections are logged here.